Orphan Medicines in Europe - 10 years on, we ask: did it work? - Available in 6 Languages
Orphan Medicines in Europe 10 years on, we ask: did it work? - Available in 6 Languages
10 years ago, the European Parliament unanimously endorsed a law to stimulate the development of treatments for rare disease patients in the EU. Since the adoption of the European orphan medicinal products legislation, 63 new treatments for rare, chronically debilitating and life-threatening diseases have received a positive EU opinion.
Did it work? We would say “yes”!