In the EU, rare diseases that are also life-threatening or chronically debilitating with a low prevalence and a high level of complexity are defined as orphan diseases.
A disease is defined as rare in Europe when it affects less than 1 in 2,000 citizens (Orphan Drug
A ‘one size fits all’ approach to the timing and methodology of appraisals will fail to take acco
It is estimated that over 6,000 rare diseases exist, although some say the actual number is close
Uncertainty in economic evaluation of innovative therapies is often managed by a call for more ev
Healthcare biotechnology refers to a medicinal or diagnostic product or a vaccine that consists o